Newsgather

pharmaceuticals

Estable8 noticias6 fuentesÚltima actualización: 16 sa önce

Últimas noticias

FDA Approves First Gene Therapy to Restore Hearing for People Born Deaf
En desarrollo
Salud·23.04.2026Resumen IA

FDA Approves First Gene Therapy to Restore Hearing for People Born Deaf

The FDA approved the first gene therapy to restore hearing for people born deaf, developed by Regeneron Pharmaceuticals. The treatment targets a rare genetic defect affecting about 50 U.S. children annually, caused by a defective OTOF gene. In clinical trials, 80% of patients achieved significant hearing restoration and 42% gained normal hearing, with effects lasting at least two years.

N
NPR News