En développement
Santé·23/04/2026Résumé IA
FDA Approves First Gene Therapy to Restore Hearing for People Born Deaf
The FDA approved the first gene therapy to restore hearing for people born deaf, developed by Regeneron Pharmaceuticals. The treatment targets a rare genetic defect affecting about 50 U.S. children annually, caused by a defective OTOF gene. In clinical trials, 80% of patients achieved significant hearing restoration and 42% gained normal hearing, with effects lasting at least two years.
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NPR News4 min de lecture