رجوعNHS to Provide Lifesaving Drugs for Children with Rare Muscle-Wasting Disease

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Guardian UK14‏/5‏/2026صحة4 د قراءةUnited Kingdom

NHS to Provide Lifesaving Drugs for Children with Rare Muscle-Wasting Disease

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NICE recommends NHS funding for nusinersen (Spinraza) and risdiplam (Evrysdi) for spinal muscular atrophy (SMA) patients in England, Wales, and Northern Ireland, offering improved survival and quality of life for hundreds of children with this rare genetic disorder.

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Hundreds of children with a rare muscle-wasting disease will be able to receive two drugs that can improve their survival in a move parents hailed as a “lifeline”. The National Institute for Health and Care Excellence (Nice) has published final draft guidance recommending that any patient who would benefit can have either drug. ... (Full article text preserved with paragraph breaks)

مواضيع ذات صلة

Spinal Muscular Atrophy

مواضيعSMA NICE NHS Spinraza Evrysdi

This article was originally published by Guardian UK.

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