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Health·1d agoAI summary
Gene Therapy for Huntington's Disease Gets New FDA Path After Official's Ouster
A gene therapy for Huntington's disease, AMT-130, has a renewed path to FDA approval after the departure of Vinay Prasad, who had previously blocked the therapy's accelerated approval process. The FDA has once again agreed that UniQure can pursue approval with trial data using standard care patients as controls, avoiding sham surgeries.
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Ars Technica